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Showing posts with the label rare diseases

Taking on the access hurdles for orphan drugs: preparing for EU HTA

Finding new treatments for ALS patients: a look at the late-stage pipeline

Turning Setbacks into Strategies: Lessons from RELYVIRO’s journey in ALS

Breaking Barriers: TECELRA Becomes the First Engineered T-Cell Therapy for Solid Tumors

Fabhalta: aprendizajes para el desarrollo exitoso de fármacos en enfermedades raras

Fabhalta: learnings for successful drug development in rare diseases